Division of Biology and Biomedical Sciences MSC 8226-13-04 660 S. Euclid Ave. St. Louis, MO 63110-1093
University of Missouri-Columbia (2019)
Molecular Genetics and Genomics
David T. Curiel, MD, PhD
Adenoviral gene therapy for MPS I
s.hurt@wustl.edu
MPS I is a lysosomal storage disease that is caused by a genetic defect in the IDUA gene with limited treatment options. I am attempting to develop a treatment for MPS I using adenoviral vectors to deliver CRISPR/Cas9 and replace the malfunctioning gene.
Last Updated: 6/24/2020 10:18:06 AM
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